AAVLife, Abbvie, Abiogen Pharma, AbMed, Abpro, Acceleron Pharma, Accelovance, Aceragen, ACMG Foundation for Genetic and Genomic Medicine, Acorda Therapeutics, Actelion, Adalvo, Adamas Pharmaceuticals, Advanced Accelerator Applications, Advaxis, Aegerion Pharmaceutical, Aevi Genomic Medicine, AFT Pharmaceuticals, Agility Clinical, Aires Pharmaceuticals, Akari Therapeutics, Akcea Therapeutics, Alcyone Lifesciences, Alexion Pharmaceuticals, Alitair Pharmaceuticals, Allergan, Almirall, Alnylam Pharmaceuticals, Amarantus BioSciences, American National Multiple Sclerosis Society, American Red Cross, AmerisourceBergen, Amicus Therapeutics, Amneal Pharmaceuticals, AmorChem, Amryt Pharma, Andromeda Biotech, AndroScience, ANI Pharmaceuticals, AOP Orphan Pharmaceuticals, Aperion Biologics, Apic Bio, Applied Genetic Technologies, Aprecia Pharmaceuticals, Aptuit, Aradigm, Arbutus, Arctic Therapeutics, Arcturus Therapeutics, Arecor, Aridis Pharmaceuticals, ArmaGen, Arphio, Array Biopharma, Asceneuron, Aslan Pharma, Astellas Pharma, AstraZeneca, Atlas Venture, Audentes Therapeutics, Auven Therapeutics, Avanzanite Bioscience, Baxalta, Beijing Double-Crane Pharmaceutical, Bellus Health, Benuvia Therapeutics, BioAlliance Pharma, BioCryst Pharmaceuticals, BioMarin Pharmaceutical, BioNTech, Bionure, BioPontis Alliance, BioSante Pharmaceuticals, BioSoteria, BioTie Therapies, BioXcel, Blood Systems, Bpifrance, BTG, Buck Institute for Age Research, California Institute for Biomedical Research, Calliditas Therapeutics, Camurus, Canadian Organization for Rare Disorders, Cancer Prevention Pharmaceuticals, Castle Creek Biosciences, Catabasis Pharmaceuticals, Catalent, Catalyst Pharmaceutical Partners, CBR International, CellAct, Cell Therapeutics, Celsion, Celsus Therapeutics, Censa Pharmaceuticals, Centocor, Centogene, Cerenis Therapeutics, Cerus, ChemoCentryx, Chiesi Farmaceutici, Children's Hospital Boston, Children's Hospital of Philadelphia, Chord Therapeutics, Chroma Therapeutics, Chugai Pharma Marketing, Clal Biotech, Clalit Health Fund, Clinigen, Cloud Pharmaceuticals, CMC Biologics, CMIC, CNS Pharmaceuticals, Confo Therapeutics, Corino Therapeutics, Cortendo, Crealta Pharmaceuticals, Critical Path Institute (C-Path), CSL Behring, Cumberland Pharmaceuticals, Cutaneous Lymphoma Foundation, Cycle Pharmaceuticals, Cyclica, Cystic Fibrosis Foundation, Cystinosis Research Foundation, Cytokinetics, D&A Pharma, DanDrit Biotech, DBV Technologies, Delta-Vir, Department of Defense, Dicerna Pharmaceuticals, Diurnal, DNAtrix, Dohmen, Drugs for Neglected Diseases Initiative, DuoCort Pharma, Edico Genome, Edimer Pharmaceuticals, Edison Pharmaceuticals, Edmond Pharma, EffRx, Eiger BioPharmaceuticals, Elan, Elixirgen, ElsaLys Biotech, Eluminex Biosciences, EMD Serono, Enable Injections, Engrail Therapeutics, EpiCept, EpiDestiny, Epirium Bio, Epivax, Erytech, Eureka Eurostars, European Commission, EUSA Pharma, Evotec, ExCEEd Orphan, Eyevance, Fast Forward, Fibrocell Science, Florida Biologix, Food and Drug Administration (FDA), Fortress Biotech, Foundation Fighting Blindness, Foundation For Angelman Syndrome Therapeutics, Fujifilm Pharma, G-treeBNT, Galena Biopharma, GBS-CIDP Foundation, Genethon, Genevant Sciences, Genomics England, Gentium, Genzyme, Gilead Sciences, Ginkgo BioWorks, GlaxoSmithKline, Global Genes, GlycoMimetics, Great Ormond Street Hospital (GOSH), Grifols, Grupo Ferrer, GtreeBNT, Halozyme Therapeutics, Harvard Medical School, Harvard University, Healthcare Royalty Partners, Hematech, HLB Therapeutics, HLS Therapeutics, Horizon Pharma plc, Houston Pharmaceuticals, Hy BioPharma, Hyperion Therapeutics, iBio, Icahn School of Medicine at Mount Sinai, Idera Pharmaceuticals, Ikano Therapeutics, Ikaria, Imaxio, ImmuneWorks, Imperial College London, In-Depth Genomics, InformedDNA, Inhibrx, Institute for the Promotion of Innovation by Science and Technology in Flanders, Intellect Neurosciences, InterMune, Invida Pharmaceuticals, Ionis Pharmaceuticals, Ipsen, Isomerase Therapeutics, Israeli National Authority for Technological Innovation, Ivax, Jackson Laboratory, Janssen Sciences, Jazz Pharmaceuticals, JCR Pharmaceuticals, John P. Hussman Foundation, Johnson & Johnson, Jupiter Orphan Therapeutics, Kadmon Pharmaceuticals, Kalon Biotherapeutics, Kalytera Therapeutics, Kamada, Kashiv BioSciences, Kentucky Bioprocessing, Kings College London, Kyowa Hakko Kirin, La Jolla Labs, Lee's Pharmaceutical, Leiden University, Lenus Therapeutics, Leukaemia & Lymphoma Research, Lexicon Pharmaceuticals, LFB Biomedicaments, LifeArc, LifeMax Laboratories, Ligand Pharmaceuticals, Longitude Capital, Lotus Tissue Repair, Lumena Pharmaceuticals, Lumos Pharma, Lumos Pharma (acquired), Lung Biotechnology, Mallinckrodt Pharmaceuticals, Marnier-Lapostolle Foundation, Massachusetts General Hospital, Mast Therapeutics, Meda, Medgenics, Medicenna Therapeutics, MedImmune, Medipal Holdings, MediWound, Medosome Biotec, Medunik Canada, Merck and Co, Mereo BioPharma, Mesoblast, Microsoft, Military Pharmaceutical Laboratory, Mills Pharmaceuticals, Minoryx Therapeutics, Mirum Pharmaceuticals, Mitsubishi Tanabe Pharma, Moulder Center for Drug Discovery Research, MSD Action Foundation (MSDAF), Mundipharma, Mustang Bio, n-Lorem Foundation, Nacuity Pharmaceuticals, NanoSonic Products, National Cancer Institute, National Health Research Institutes, National Institute of Diabetes and Digestive and Kidney Diseases, National Institute of Neurological Disorders and Stroke, National Institutes of Health, National Organization for Rare Disorders, Nestle Health Science, Neuraxpharm, Neurotrope BioScience, NeuroVive Pharmaceutical, Newron Pharmaceuticals, NIH Undiagnosed Diseases Program, Nimbus Apollo, Nippon Chemiphar, NMI TT Pharmaservices, Novartis, Novasep, NovelMed, Noventia Pharma, NovImmune, Novo Nordisk, OcuNexus Therapeutics, OncoPep, OncoSec Medical, Oncosynergy, Onxeo, Ophthotech, OPKO Health, Oraxion Therapeutics, Orchard Therapeutics, OrphanDev, Orphan Europe, OrphanPacific, Orphan Therapeutics, Orphatec Pharmaceuticals, Orphazyme, Orphic Therapeutics, Oryzon, OSI Pharmaceuticals, Oxford BioMedica, Parent Project Muscular Dystrophy, PellePharm, Penn State Research Foundation, PerkinElmer, Perlara, Pfizer, PharmaMar, Pharming Group, Pharnext, Piramal, Plexcera, PoC Capital, Population Diagnostics, Presidio Pharmaceuticals, Progeria Research Foundation, Prometic Life Sciences, ProQR Therapeutics, Proteostasis Therapeutics, ProThera, PSR Orphan Drug Experts, PTC Therapeutics, Qiagen, Queen Mary University of London, R-Tech Ueno, Radius Health, Ramot at Tel Aviv University, Rare Disease Company Coalition, Rare Expertise, RCC Pharma, Receptos, Recipharm, Recursion, Regenerx, Regenxbio, ReGenX Biosciences, Regulus Therapeutics, Replica Analytics, Repligen, Resverlogix, Retinagenix, Retrophin, RetroSense Therapeutics, Rett Syndrome Research Trust, Rezolute, Rhythm Pharmaceuticals, Rigi Healthcare, Rigi Orphan, Roche, Rocket Pharmaceuticals, S*Bio, Sagent Pharmaceuticals, Saint Louis University, Sanofi, Savara Pharma, Savient Pharmaceuticals, Scioderm, SCOUT, Selecta Biosciences, Selexis, Sentinel Oncology, Seres Therapeutics, Shenzhen Hepalink Pharmaceutical, Shire Human Genetic Therapies, Shire Laboratories, Shire Pharmaceuticals, SIFI (Societa Industria Farmaceutica Italiana), Sirenas, Sirtex Medical, SK Biopharmaceuticals, Sol-Gel, Soleno Therapeutics, Soligenix, SOM Biotech, Spark Therapeutics, SpePharm, Sperogenix Therapeutics, Spooner Girls Foundation, St. Jude Children's Research Hospital, STADA Arzneimittel, Stanford University, Stealth BioTherapeutics, Stealth Therapeutics, Sucampo AG, Sucampo Pharmaceuticals, Sumitomo Dainippon Pharma, Swedish Orphan, Swedish Orphan Biovitrum, Swixx Biopharma, SymbioTec, Synageva BioPharma, SynCo Bio Partners, Taisho Pharmaceutical, Takeda America Holdings, Takeda Pharmaceutical, Tamid Bio, Taysha Gene Therapies, Teva Pharmaceutical Industries, Texas A&M University, Therapyx, Theratechnologies, Tillotts Pharma, Timber Pharmaceuticals, TNI BioTech, TopoTarget, Translational Medicine Accelerator, Turgut Ilaclari, TWi Biotechnology, twoXAR, Tyris Therapeutics, Ucyclyd Pharma, UH Harrington Discovery Institute, Ultragenyx Pharmaceuticals, UniQure, Universite Laval, University College Dublin, University College London, University of Birmingham, University of California Irvine, University of California Los Angeles, University of Cambridge, University of Florida, University of Manchester, University of North Carolina, University of Oxford, University of Pennsylvania, University of Pennsylvania Center for Orphan Disease Research and Therapy, University of Quebec, University of Southern California, Upsher-Smith, UT Southwestern Medical Center, Valeant Pharmaceuticals, Vanderbilt University, Vaxil BioTherapeutics, Veeva Systems, Vericel, VIB, Videregen, Viela Bio, Vifor Pharma, Viking Therapeutics, Viropharma, Vivalis, Vivet Therapeutics, Volution Immuno Pharma, Vtesse, Wellstat Therapeutics, Winhealth Pharma Group, World Orphan Drug Alliance, WuXi Biologics, X-chem, Xenetic Biosciences, Xenon Pharmaceuticals, XERIS Pharmaceuticals, Xoma, Yungjin Pharmaceutical, YuYang DNU, Zacharon Pharmaceuticals, Zhejiang Hisun Pharmaceutical